Last update 14 Jun 2025

Gene Therapy (Genetics Institute/Targeted Genetics)

Overview

Basic Info

Drug Type
AAV based gene therapy
Synonyms
gene therapy (Genetics Institute/Targeted Genetics)
Target
F8
Action
stimulants
Mechanism
F8 stimulants(Coagulation factor VIII stimulants)
Therapeutic Areas
Congenital DisordersHemic and Lymphatic DiseasesOther Diseases
Active Indication-
Inactive Indication
Hemophilia A
Originator Organization
The Rockefeller UniversityThe Rockefeller University
Active Organization-
Inactive Organization
The University of North Carolina at Chapel HillThe University of North Carolina at Chapel HillThe Rockefeller UniversityThe Rockefeller UniversityArmata Pharmaceuticals, Inc.Armata Pharmaceuticals, Inc.
License Organization-
Drug Highest PhasePendingDiscovery
First Approval Date-
Regulation-

Related

100 Clinical Results associated with Gene Therapy (Genetics Institute/Targeted Genetics)
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100 Translational Medicine associated with Gene Therapy (Genetics Institute/Targeted Genetics)
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100 Patents (Medical) associated with Gene Therapy (Genetics Institute/Targeted Genetics)
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100 Deals associated with Gene Therapy (Genetics Institute/Targeted Genetics)
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R&D Status

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IndicationHighest PhaseCountry/LocationOrganizationDate
Hemophilia ADiscovery
United States
Armata Pharmaceuticals, Inc.Armata Pharmaceuticals, Inc.
-
Hemophilia ADiscovery
United States
The Rockefeller UniversityThe Rockefeller University
-
Hemophilia ADiscovery
United States
The University of North Carolina at Chapel HillThe University of North Carolina at Chapel Hill
-
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Clinical Result

Indication
Phase
Evaluation
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Study
Phase
PopulationAnalyzed EnrollmentGroupResultsEvaluationPublication Date

No Data

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Deal

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Core Patent

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Clinical Trial

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Approval

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Regulation

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