Drug Type ASO |
Synonyms- |
Target |
Action inhibitors |
Mechanism ABCA4 inhibitors(ATP binding cassette subfamily A member 4 inhibitors) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
License Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
RegulationOrphan Drug (European Union) |

| Indication | Highest Phase | Country/Location | Organization | Date |
|---|---|---|---|---|
| Stargardt Disease | Preclinical | Netherlands | 01 Dec 2025 |





