Drug Type AAV based gene therapy |
Synonyms adeno-associated viral vector-based gene therapy (Real Regulatory Limited) |
Target- |
Action- |
Mechanism Gene transference |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
License Organization- |
Drug Highest PhaseDiscovery |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Neuronal Ceroid-Lipofuscinoses | Discovery | Ireland | - |