Last update 27 Jun 2026

Dystrophin replacement therapy(Orna)

Overview

Basic Info

Drug Type
circular RNA
Synonyms-
Target
dystrophin
Action
modulators
Mechanism
dystrophin modulators(Dystrophin modulators)
Therapeutic Areas
Nervous System DiseasesCongenital DisordersSkin and Musculoskeletal Diseases+ [1]
Active Indication
Muscular Dystrophy, Duchenne
Inactive Indication-
Originator Organization
Orna Therapeutics, Inc.Orna Therapeutics, Inc.
Active Organization
Renagade Thera
Inactive Organization
Orna Therapeutics, Inc.Orna Therapeutics, Inc.
License Organization-
Drug Highest PhaseDiscovery
First Approval Date-
Regulation-

Related

100 Clinical Results associated with Dystrophin replacement therapy(Orna)
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100 Translational Medicine associated with Dystrophin replacement therapy(Orna)
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100 Patents (Medical) associated with Dystrophin replacement therapy(Orna)
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100 Deals associated with Dystrophin replacement therapy(Orna)
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R&D Status

10 top R&D records.
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IndicationHighest PhaseCountry/LocationOrganizationDate
Muscular Dystrophy, DuchenneDiscovery
United States
Orna Therapeutics, Inc.Orna Therapeutics, Inc.
13 Apr 2023
Muscular Dystrophy, DuchenneDiscovery
United States
Renagade Thera
13 Apr 2023
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Clinical Result

Indication
Phase
Evaluation
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Phase
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Deal

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Clinical Trial

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Approval

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Regulation

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