Acquisition
License out/in
28 Feb 2026
Jaguar Gene Therapy Announces Successful Completion of Dosing of First Patient Cohort in Clinical Trial Evaluating JAG201 for the Treatment of a Leading Monogenic Cause of Autism Spectrum Disorder Known as Phelan-McDermid Syndrome
Orphan DrugFast TrackClinical Study
Cartography Biosciences Doses First Patient in Phase 1 Trial of CBI-1214, a Highly Specific T-Cell Engager for the Treatment of Colorectal Cancer
ImmunotherapyAACR
27 Feb 2026
HekaBio and Alpha Tau Medical Obtain Approval in Japan for Solid Tumor Treatment Alpha DaRT
Radiation TherapyDrug ApprovalClinical Study
IntraBio Receives Positive European Medicines Agency Opinion for Orphan Medicinal Product Designation for Acetylleucine for CACNA1A Disorders
Drug ApprovalOrphan Drug
27 Feb 2026
ImmunotherapyClinical Study
27 Feb 2026
27 Feb 2026
Azafaros Announces Publication of Preclinical Efficacy Data with Nizubaglustat in GM2 Gangliosidosis
Orphan DrugFast TrackClinical Result
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