11 hours ago
11 hours ago
Immunotherapy
10 Feb 2026
Clinical Result
10 Feb 2026
Clinical StudyCollaborate
10 Feb 2026
10 Feb 2026
Drug Approval
Zevra Therapeutics Presents Positive New Real-World Data on MIPLYFFA® in Patients with Neimann-Pick Disease Type C (NPC) at the 22nd Annual WORLDSymposium™
Clinical ResultDrug ApprovalOrphan Drug
Clinical Result
Clinical Result
Clinical ResultOrphan DrugGene TherapyFast TrackClinical Study
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