Drug Type AAV based gene therapy |
Synonyms BBP-818 |
Target |
Mechanism GALT modulators(Galactose-1-phosphate uridylyltransferase modulators) |
Therapeutic Areas |
Active Indication- |
Inactive Indication |
Originator Organization |
Active Organization- |
Inactive Organization |
Drug Highest PhaseDiscontinuedPreclinical |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Galactosemias | Preclinical | US | - |