Drug Type AAV based gene therapy |
Synonyms |
Target- |
Mechanism Gene modulators |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Angelman Syndrome | Preclinical | JP | - | |
Central Nervous System Diseases | Preclinical | JP | - |