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Last update 15 Sep 2025
Pitt Hopkins treatment gene therapy(MAHZI Therapeutics)
Last update 15 Sep 2025
Overview
Basic Info
Drug Type Gene therapy |
Synonyms- |
Target |
Action modulators |
Mechanism TCF4 modulators(transcription factor 4 modulators) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
License Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
Regulation- |
R&D Status
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| Indication | Highest Phase | Country/Location | Organization | Date |
|---|---|---|---|---|
| Pitt-Hopkins Syndrome | Preclinical | United States | 01 Sep 2024 |
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Clinical Result
Clinical Result
Indication
Phase
Evaluation
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