Drug Type AAV based gene therapy |
Synonyms |
Target |
Action stimulants |
Mechanism GLA stimulants(α-Galactosidase stimulants) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePhase 1/2 |
First Approval Date- |
RegulationOrphan Drug (United States) |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Fabry Disease | Phase 2 | China | 16 Dec 2024 |