100 Clinical Results associated with Canine AAV8-MTM1 vector
100 Translational Medicine associated with Canine AAV8-MTM1 vector
100 Patents (Medical) associated with Canine AAV8-MTM1 vector
1
Literatures (Medical) associated with Canine AAV8-MTM1 vector22 Jan 2014·Science translational medicineQ1 · MEDICINE
Gene Therapy Prolongs Survival and Restores Function in Murine and Canine Models of Myotubular Myopathy
Q1 · MEDICINE
Article
Author: Martin K. Childers ; Thomas Soker ; Thibaud Jamet ; Alan H. Beggs ; J. Koudy Williams ; Caroline Hammer ; Alban Vignaud ; Laetitia Van Wittenberghe ; Samia Martin ; Melissa Goddard ; Mark E. Furth ; Carole Masurier ; Xuan Guan ; Robert W. Grange ; David L. Mack ; Anna Buj-Bello ; Mandy Lockard ; Nathalie Danièle ; Fulvio Mavilio ; Christel Rivière ; Jane Barber ; Michael W. Lawlor ; Jonathan A. Doering ; Erin Mitchell ; Romain Joubert ; Christelle Moal ; Karine Poulard ; Branden E. Rider ; Philippe Moullier
Intravenous injection of an adeno-associated viral vector expressing the myotubularin (
MTM1
) gene improves survival and rescues skeletal muscle function in mice and dogs affected by myotubular myopathy.
100 Deals associated with Canine AAV8-MTM1 vector