Drug Type AAV based gene therapy |
Synonyms RC 0125, RC0125 |
Target |
Action modulators |
Mechanism TRPV4 modulators(Transient receptor potential cation channel subfamily V member 4 modulators) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
License Organization- |
Drug Highest PhaseDiscovery |
First Approval Date- |
Regulation- |
| Indication | Highest Phase | Country/Location | Organization | Date |
|---|---|---|---|---|
| Charcot-Marie-Tooth Disease, Type 2C | Discovery | South Korea | 01 Jun 2026 | |
| Musculoskeletal Abnormalities | Discovery | South Korea | 01 Jun 2026 | |
| Osteochondrodysplasias | Discovery | South Korea | 01 Jun 2026 | |
| Spinal Curvatures | Discovery | South Korea | 01 Jun 2026 |





