Drug Type Transformer Base Editor |
Synonyms- |
Target |
Action inhibitors |
Mechanism ADAR inhibitors(adenosine deaminase RNA specific inhibitors) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Mucopolysaccharidosis I | Preclinical | China | 26 Mar 2025 | |
Mucopolysaccharidosis I | Preclinical | China | 26 Mar 2025 |