Drug Type AAV based gene therapy |
Synonyms AAV5-RDH12, AAV-RDH12 |
Target |
Action modulators |
Mechanism RDH12 modulators(retinol dehydrogenase 12 modulators), Gene transference(Gene transference) |
Therapeutic Areas |
Active Indication- |
Inactive Indication |
Originator Organization |
Active Organization- |
Inactive Organization |
License Organization- |
Drug Highest PhaseDiscontinuedPreclinical |
First Approval Date- |
Regulation- |
| Indication | Highest Phase | Country/Location | Organization | Date |
|---|---|---|---|---|
| Leber Congenital Amaurosis | Preclinical | United States | 01 Feb 2022 | |
| Retinal Dystrophies | Preclinical | United States | 01 Feb 2022 |





