Drug Type AAV based gene therapy |
Synonyms AAV-RDH12 |
Target |
Mechanism RDH12 modulators(retinol dehydrogenase 12 modulators), Gene transference |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Leber Congenital Amaurosis | Preclinical | US | - | |
Retinal Dystrophies | Preclinical | US | - |