Last update 07 Nov 2024
VGM-R02b
Last update 07 Nov 2024
Overview
Basic Info
Drug Type AAV based gene therapy |
Synonyms adeno-associated viral vector 9 delivering human Glutaryl-CoA Dehydrogenase (GCDH) gene |
Target |
Mechanism GCDH stimulants(glutaryl-CoA dehydrogenase stimulants) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePhase 1 |
First Approval Date- |
RegulationOrphan Drug (US), Orphan Drug (EU) |
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Related
2
Clinical Trials associated with VGM-R02bAn Open-Label, Dose-Escalation and Dose-Expansion Phase I Clinical Study to Evaluate the Tolerability, Safety and Efficacy of VGM-R02b in Patients With Glutaric Acidemia Type I
一项评估在I型戊二酸血症患者中给予VGM-R02b后的耐受性、安全性和有效性的开放、剂量递增和剂量扩展的I期临床研究
[Translation] An open-label, dose-escalation, and dose-expansion Phase I study evaluating the tolerability, safety, and efficacy of VGM-R02b in patients with glutaric acidemia type I
100 Clinical Results associated with VGM-R02b
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100 Translational Medicine associated with VGM-R02b
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100 Patents (Medical) associated with VGM-R02b
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100 Deals associated with VGM-R02b
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R&D Status
10 top R&D records. to view more data
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| Indication | Highest Phase | Country/Location | Organization | Date |
|---|---|---|---|---|
| Glutaric Acidemia I | Phase 1 | CN | 25 Dec 2023 |
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