Drug Type AAV based gene therapy |
Synonyms |
Target |
Mechanism ABCA4 modulators(ATP binding cassette subfamily A member 4 modulators) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePhase 1/2 |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Stargardt Disease | Phase 2 | CN | 20 Nov 2023 |