Drug Type Enzyme |
Synonyms ARSA, Arylsulfatase A(Linno Pharmaceuticals), Recombinant fusion protein composed of a recombinant human arylsulfatase A (rhARSA) fused with a variable domain of the heavy chain of heavy chain-only antibody fragment targeting human transferrin + [3] |
Target |
Mechanism ASA replacements(Cerebroside sulfatase replacements) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
RegulationOrphan Drug (US) |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Leukodystrophy, Metachromatic | Preclinical | US | 15 Dec 2023 |