Drug Type Gene therapy |
Synonyms- |
Target |
Action modulators |
Mechanism DARS2 modulators(aspartyl-tRNA synthetase 2, mitochondrial modulators) |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
License Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
Regulation- |
| Indication | Highest Phase | Country/Location | Organization | Date |
|---|---|---|---|---|
| Leukoencephalopathy With Brainstem and Spinal Cord Involvement and Lactate Elevation | Preclinical | United States | 13 May 2025 |





