Drug Type AAV based gene therapy  | 
Synonyms-  | 
Target  | 
Action inhibitors  | 
Mechanism mTOR inhibitors(Serine/threonine-protein kinase mTOR inhibitors), Gene transference(Gene transference)  | 
Therapeutic Areas  | 
Active Indication  | 
Inactive Indication-  | 
Originator Organization  | 
Active Organization  | 
Inactive Organization-  | 
License Organization-  | 
Drug Highest PhasePreclinical  | 
First Approval Date-  | 
Regulation-  | 
| Indication | Highest Phase | Country/Location | Organization | Date | 
|---|---|---|---|---|
| Hemophilia A | Preclinical | United States   | - | |
| Hemophilia A | Preclinical | United States   | - | 





