Drug Type AAV based gene therapy |
Synonyms AAV8 ATP7B gene therapy (Aligen Therapeutics) |
Target |
Mechanism ATP7B gene stimulants(ATPase copper transporting beta gene stimulants), Gene transference |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Hepatolenticular Degeneration | Preclinical | ES | - | |
Hepatolenticular Degeneration | Preclinical | ES | - |