Drug Type AAV based gene therapy |
Synonyms AAV.Anc80.hRPGRIP1, OT-004, RP-GRIP1 |
Target- |
Mechanism Gene transference |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
RegulationOrphan Drug (US) |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Leber Congenital Amaurosis | Preclinical | US | 01 Jul 2019 | |
Retinal Dystrophies | Discovery | US | - | |
Retinal Dystrophies | Discovery | US | - |