Drug Type ASO |
Synonyms SCN8A splicing targeted SMOs (LifeSplice Pharma) |
Target |
Mechanism Nav1.6 blockers(Sodium channel protein type VIII alpha subunit blockers) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
CDKL5 Deficiency Disorder | Preclinical | US | - |