Last update 08 May 2025

AAV5-hCNGB1 gene (NIH/NCATS)

Overview

Basic Info

Drug Type
AAV based gene therapy
Synonyms
recombinant adeno-associated virus 5 vector expressing a functional human cyclic nucleotide gated channel subunit beta 1 (CNGB1) gene (NIH/NCATS)
Target
CNGB1
Action
modulators
Mechanism
CNGB1 modulators(cyclic nucleotide gated channel subunit beta 1 modulators)
Therapeutic Areas
Congenital DisordersEye DiseasesOther Diseases
Active Indication
Retinitis Pigmentosa
Inactive Indication-
Originator Organization
National Center for Advancing Translational SciencesNational Center for Advancing Translational SciencesNational Institutes of HealthNational Institutes of Health
Active Organization
National Center for Advancing Translational SciencesNational Center for Advancing Translational SciencesNational Institutes of HealthNational Institutes of Health
Inactive Organization-
License Organization-
Drug Highest PhasePreclinical
First Approval Date-
RegulationOrphan Drug (United States)

Related

100 Clinical Results associated with AAV5-hCNGB1 gene (NIH/NCATS)
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100 Translational Medicine associated with AAV5-hCNGB1 gene (NIH/NCATS)
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100 Patents (Medical) associated with AAV5-hCNGB1 gene (NIH/NCATS)
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100 Deals associated with AAV5-hCNGB1 gene (NIH/NCATS)
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R&D Status

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IndicationHighest PhaseCountry/LocationOrganizationDate
Retinitis PigmentosaPreclinical
United States
National Center for Advancing Translational SciencesNational Center for Advancing Translational Sciences
23 Sep 2024
Retinitis PigmentosaPreclinical
United States
National Institutes of HealthNational Institutes of Health
23 Sep 2024
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Clinical Result

Indication
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Deal

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Clinical Trial

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Approval

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Regulation

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