Drug Type Gene therapy |
Synonyms |
Target |
Mechanism Cep290 modulators(Centrosomal protein of 290 kDa modulators) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Leber Congenital Amaurosis 10 | Preclinical | US | - |