Last update 05 Nov 2025

Human hydroxymethylbilane synthase encoding mRNA(Moderna Therapeutics)

Overview

Basic Info

Drug Type
mRNA
Synonyms
hPBGD mRNA Moderna Therapeutics, hPBGD mRNA(Moderna)
Target
PBGD
Action
modulators
Mechanism
PBGD modulators(Porphobilinogen deaminase modulators)
Therapeutic Areas
Congenital DisordersDigestive System DisordersEndocrinology and Metabolic Disease+ [2]
Active Indication
Porphyria, Acute Intermittent
Inactive Indication-
Originator Organization
Moderna, Inc.Moderna, Inc.
Active Organization
University of NavarraUniversity of NavarraModerna, Inc.Moderna, Inc.
Inactive Organization
Center for Applied Medical Research
License Organization-
Drug Highest PhasePreclinical
First Approval Date-
Regulation-

Related

100 Clinical Results associated with Human hydroxymethylbilane synthase encoding mRNA(Moderna Therapeutics)
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100 Translational Medicine associated with Human hydroxymethylbilane synthase encoding mRNA(Moderna Therapeutics)
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100 Patents (Medical) associated with Human hydroxymethylbilane synthase encoding mRNA(Moderna Therapeutics)
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100 Deals associated with Human hydroxymethylbilane synthase encoding mRNA(Moderna Therapeutics)
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R&D Status

10 top R&D records.
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IndicationHighest PhaseCountry/LocationOrganizationDate
Porphyria, Acute IntermittentPreclinical
United States
Moderna, Inc.Moderna, Inc.
04 Oct 2024
Porphyria, Acute IntermittentPreclinical
Spain
University of NavarraUniversity of Navarra
04 Oct 2024
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Clinical Result

Indication
Phase
Evaluation
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Study
Phase
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Deal

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Core Patent

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Clinical Trial

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Approval

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Regulation

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