Drug Type AAV based gene therapy |
Synonyms |
Target |
Mechanism ATP7B gene stimulants(ATPase copper transporting beta gene stimulants) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhaseIND Application |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Hepatolenticular Degeneration | IND Application | CN | 14 Nov 2024 | |
Neuromuscular Diseases | Discovery | CN | - |