Drug Type Small molecule drug |
Synonyms S 606001, S606001 |
Target |
Action inhibitors |
Mechanism GYS1 gene inhibitors |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
License Organization- |
Drug Highest PhasePhase 2 |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Glycogen Storage Disease Type II | Phase 2 | United States | 30 Oct 2025 | |
Glycogen Storage Disease Type II | Phase 2 | Belgium | 30 Oct 2025 | |
Glycogen Storage Disease Type II | Phase 2 | Denmark | 30 Oct 2025 | |
Glycogen Storage Disease Type II | Phase 2 | France | 30 Oct 2025 | |
Glycogen Storage Disease Type II | Phase 2 | Germany | 30 Oct 2025 | |
Glycogen Storage Disease Type II | Phase 2 | Italy | 30 Oct 2025 | |
Glycogen Storage Disease Type II | Phase 2 | Netherlands | 30 Oct 2025 | |
Glycogen Storage Disease Type II | Phase 2 | Spain | 30 Oct 2025 | |
Glycogen Storage Disease Type II | Phase 2 | United Kingdom | 30 Oct 2025 |