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Last update 13 Dec 2025
ABCA4 gene editing therapy (Beam Therapeutics)
Last update 13 Dec 2025
Overview
Basic Info
Drug Type AAV based gene therapy |
Synonyms- |
Target |
Action stimulants |
Mechanism ABCA4 stimulants(ATP binding cassette subfamily A member 4 stimulants), Gene transference(Gene transference) |
Therapeutic Areas |
Active Indication- |
Inactive Indication |
Originator Organization |
Active Organization- |
Inactive Organization |
License Organization- |
Drug Highest PhaseDiscontinuedDiscovery |
First Approval Date- |
Regulation- |
R&D Status
10 top R&D records. to view more data
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| Indication | Highest Phase | Country/Location | Organization | Date |
|---|---|---|---|---|
| Stargardt Disease 4 | Discovery | United States | - |
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Clinical Result
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