Last update 14 Jun 2025

AAV8-MFRP

Overview

Basic Info

Drug Type
AAV based gene therapy
Synonyms
Adeno-Associated Virus Serotype 8 carrying the Membrane Frizzled Related Protein (MFRP) transgene
Target
MFRP
Action
modulators
Mechanism
MFRP modulators(membrane frizzled-related protein modulators)
Therapeutic Areas
Congenital DisordersEye DiseasesOther Diseases
Active Indication
Retinal Dystrophies
Inactive Indication-
Originator Organization
The Trustees of Columbia University in The City of New YorkThe Trustees of Columbia University in The City of New York
Active Organization
The Trustees of Columbia University in The City of New YorkThe Trustees of Columbia University in The City of New York
Inactive Organization-
License Organization-
Drug Highest PhasePreclinical
First Approval Date-
RegulationOrphan Drug (United States)

Related

100 Clinical Results associated with AAV8-MFRP
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100 Translational Medicine associated with AAV8-MFRP
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100 Patents (Medical) associated with AAV8-MFRP
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100 Deals associated with AAV8-MFRP
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R&D Status

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IndicationHighest PhaseCountry/LocationOrganizationDate
Retinal DystrophiesPreclinical
United States
The Trustees of Columbia University in The City of New YorkThe Trustees of Columbia University in The City of New York
10 Jun 2025
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Clinical Result

Indication
Phase
Evaluation
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Phase
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Deal

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Clinical Trial

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Approval

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Regulation

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