Drug Type AAV based gene therapy |
Synonyms AAV-Ep+(Latus Bio) |
Target |
Action modulators |
Mechanism TPP1 modulators(Tripeptidyl Peptidase 1 modulators) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Neuronal Ceroid-Lipofuscinoses | Preclinical | United States | 07 May 2024 | |
Ceroid Lipofuscinosis, Neuronal, 2 | Preclinical | United States | 02 May 2024 |