Drug Type Gene therapy, Hematopoietic stem cell therapy |
Synonyms autologous CD34+ cells transduced with a lentiviral vector containing the human RAG1 gene, MB 110 - Mustang Bio, MB-110 - Mustang Bio + [7] |
Target |
Mechanism RAG-1 stimulants(recombination activating 1 stimulants) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePhase 1/2 |
First Approval Date- |
RegulationOrphan Drug (US) |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Severe Combined Immunodeficiency | Phase 2 | NL | 22 Jul 2022 |