Drug Type AAV based gene therapy |
Synonyms arylsulfatase A gene therapy (INSERM) |
Target- |
Action- |
Mechanism Gene transference |
Therapeutic Areas |
Active Indication- |
Inactive Indication |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Leukodystrophy, Metachromatic | Phase 2 | France | 22 Mar 2013 |