Drug Type AAV based gene therapy |
Synonyms arylsulfatase A gene therapy (INSERM) |
Target- |
Action- |
Mechanism Gene transference |
Therapeutic Areas |
Active Indication- |
Inactive Indication |
| Indication | Highest Phase | Country/Location | Organization | Date |
|---|---|---|---|---|
| Leukodystrophy, Metachromatic | Phase 2 | France | 22 Mar 2013 |





