Last update 21 Oct 2025

Elpida-02

Overview

Basic Info

Drug Type
AAV based gene therapy
Synonyms
AAV9 gene therapy containing codon optimized human FIG4 cDNA coding sequence (Elpida Therapeutics), AAV9-hFIG4 (Elpida Therapeutics), Elpida 02
Target
FIG4
Action
modulators
Mechanism
FIG4 modulators(FIG4 phosphoinositide 5-phosphatase modulators)
Therapeutic Areas
Nervous System DiseasesCongenital DisordersOther Diseases
Active Indication
Charcot-Marie-Tooth Disease, Type 4j
Inactive Indication-
Originator Organization
Elpida TherapeuticsElpida Therapeutics
Active Organization
Elpida TherapeuticsElpida Therapeutics
Inactive Organization-
License Organization
Elpida TherapeuticsElpida TherapeuticsViralgen Vector Core SLViralgen Vector Core SL
Drug Highest PhasePreclinical
First Approval Date-
RegulationOrphan Drug (United States)

Related

100 Clinical Results associated with Elpida-02
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100 Translational Medicine associated with Elpida-02
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100 Patents (Medical) associated with Elpida-02
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100 Deals associated with Elpida-02
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R&D Status

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IndicationHighest PhaseCountry/LocationOrganizationDate
Charcot-Marie-Tooth Disease, Type 4jPreclinical
United States
Elpida TherapeuticsElpida Therapeutics
08 Oct 2023
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Clinical Result

Indication
Phase
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Study
Phase
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Deal

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Core Patent

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Clinical Trial

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Approval

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Regulation

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