Drug Type Gene therapy, Hematopoietic stem cell therapy |
Synonyms |
Target |
Action modulators |
Mechanism β-globin modulators(Hemoglobin beta chain modulators) |
Therapeutic Areas |
Active Indication |
Inactive Indication |
Originator Organization |
Active Organization |
Inactive Organization |
License Organization- |
Drug Highest PhasePhase 2 |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Thalassemia | Phase 2 | - | - | |
Beta-Thalassemia | Preclinical | Italy | 01 May 2015 | |
Beta-Thalassemia | Preclinical | Italy | 01 May 2015 | |
Transfusion-dependent Beta Thalassemia | Preclinical | Italy | 01 May 2015 | |
Transfusion-dependent Beta Thalassemia | Preclinical | Italy | 01 May 2015 |