Drug Type AAV based gene therapy |
Synonyms OPGx BEST1 |
Target |
Mechanism BEST1 modulators(Bestrophin-1 modulators) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePhase 1/2 |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Vitelliform Macular Dystrophy | Phase 2 | - | - | |
Retinal Dystrophies | Preclinical | US | 06 Mar 2024 |