Drug Type AAV based gene therapy |
Synonyms- |
Target |
Action stimulants |
Mechanism ATP7B gene stimulants(ATPase copper transporting beta gene stimulants), Gene transference(Gene transference) |
Therapeutic Areas |
Active Indication- |
Inactive Indication |
Originator Organization |
Active Organization- |
Inactive Organization |
License Organization- |
Drug Highest PhaseDiscontinuedPreclinical |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Hepatolenticular Degeneration | Preclinical | United States | - |