Drug Type AAV based gene therapy |
Synonyms ADAR2 gene therapy (GTRI) |
Target |
Mechanism ADARB1 inhibitors(adenosine deaminase RNA specific B1 inhibitors), Gene transference |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePhase 1/2 |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Amyotrophic Lateral Sclerosis | Phase 2 | JP | 07 Jun 2023 |