Request Demo
Last update 24 May 2025
Cystic fibrosis gene therapy(Copernicus Therapeutics, Inc.)
Last update 24 May 2025
Overview
Basic Info
Drug Type Gene therapy |
Synonyms Compacted DNA, DNA nanoparticle gene therapy, Plasmid DNA vector expressing cystic fibrosis transmembrane gene + [1] |
Target |
Action stimulants |
Mechanism CFTR stimulants(Cystic fibrosis transmembrane conductance regulator stimulants) |
Therapeutic Areas |
Active Indication- |
Inactive Indication |
Originator Organization |
Active Organization- |
Inactive Organization |
License Organization- |
Drug Highest PhasePendingPhase 2 |
First Approval Date- |
RegulationOrphan Drug (United States) |
Login to view timeline
R&D Status
10 top R&D records. to view more data
Login
| Indication | Highest Phase | Country/Location | Organization | Date |
|---|---|---|---|---|
| Cystic Fibrosis | Phase 2 | United States | 20 Jan 2003 |
Login to view more data
Clinical Result
Clinical Result
Indication
Phase
Evaluation
View All Results
Not Applicable | - | - | (Transtracheal application of sec-R targeted compacted pCMV FIX plasmid) | imaqeboxxk(qzejmtszrf) = clzfqofsat pxwrkonqga (ayahralzsq ) | - | 01 May 2004 | |
(Sec-R targeted pCMV FIX injected intravenously via the tail vein) | imaqeboxxk(qzejmtszrf) = ebxlpyyaia pxwrkonqga (ayahralzsq ) | ||||||
Phase 1/2 | Cystic Fibrosis basal nasal potential difference (NPD) | FEV1 | 12 | CFTR001 Gene Transfer Vector (Compacted DNA in Saline) | ocjqbriots(cfslrcfnlc) = all other adverse events were grade I in severity, and none were felt to be due to compacted DNA exposure sfmpcsaxxj (ncgjrqwdls ) View more | Positive | 01 May 2003 |
Login to view more data
Translational Medicine
Boost your research with our translational medicine data.
login
or
Deal
Boost your decision using our deal data.
login
or
Core Patent
Boost your research with our Core Patent data.
login
or
Clinical Trial
Identify the latest clinical trials across global registries.
login
or
Approval
Accelerate your research with the latest regulatory approval information.
login
or
Regulation
Understand key drug designations in just a few clicks with Synapse.
login
or
AI Agents Built for Biopharma Breakthroughs
Accelerate discovery. Empower decisions. Transform outcomes.
Get started for free today!
Accelerate Strategic R&D decision making with Synapse, PatSnap’s AI-powered Connected Innovation Intelligence Platform Built for Life Sciences Professionals.
Start your data trial now!
Synapse data is also accessible to external entities via APIs or data packages. Empower better decisions with the latest in pharmaceutical intelligence.
Bio
Bio Sequences Search & Analysis
Sign up for free
Chemical
Chemical Structures Search & Analysis
Sign up for free