Last update 21 Nov 2024
Angelman Syndrome (HuidaGene)
Last update 21 Nov 2024
Overview
Basic Info
Drug Type AAV based gene therapy |
Synonyms AAV Vectors Packaged hfCas13Y or hfCas12Max (HuidaGene) |
Target |
Mechanism Ube3a-ATS modulators(small nucleolar RNA host gene 14 modulators) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
Regulation- |
R&D Status
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| Indication | Highest Phase | Country/Location | Organization | Date |
|---|---|---|---|---|
| Angelman Syndrome | Preclinical | CN | 07 May 2024 |
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Clinical Result
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