Last update 09 May 2026

APRTX-001

Overview

Basic Info

Drug Type
ASO
Synonyms
APRTX 001, APRTX001
Target
CD33
Action
inhibitors
Mechanism
CD33 inhibitors(Myeloid cell surface antigen CD33 inhibitors)
Therapeutic Areas
Nervous System DiseasesEndocrinology and Metabolic DiseaseOther Diseases
Active Indication
Alzheimer DiseaseAmyotrophic Lateral SclerosisFrontotemporal Dementia
Inactive Indication-
Originator Organization
Aperture Therapeutics, Inc.Aperture Therapeutics, Inc.
Active Organization
Aperture Therapeutics, Inc.Aperture Therapeutics, Inc.
Inactive Organization-
License Organization-
Drug Highest PhaseIND Application
First Approval Date-
Regulation-
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Structure/Sequence

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Related

100 Clinical Results associated with APRTX-001
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100 Translational Medicine associated with APRTX-001
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100 Patents (Medical) associated with APRTX-001
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100 Deals associated with APRTX-001
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R&D Status

10 top R&D records.
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IndicationHighest PhaseCountry/LocationOrganizationDate
Alzheimer DiseasePreclinical
United States
Aperture Therapeutics, Inc.Aperture Therapeutics, Inc.
01 Dec 2025
Amyotrophic Lateral SclerosisPreclinical
United States
Aperture Therapeutics, Inc.Aperture Therapeutics, Inc.
01 Dec 2025
Frontotemporal DementiaPreclinical
United States
Aperture Therapeutics, Inc.Aperture Therapeutics, Inc.
01 Dec 2025
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Clinical Result

Indication
Phase
Evaluation
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Study
Phase
PopulationAnalyzed EnrollmentGroupResultsEvaluationPublication Date

No Data

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Deal

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Core Patent

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Clinical Trial

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Approval

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Regulation

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