Drug Type ASO |
Synonyms ION-648402 |
Target |
Action inhibitors |
Mechanism GYS1 gene inhibitors |
Therapeutic Areas |
Active Indication- |
Inactive Indication |
Originator Organization |
Active Organization- |
Inactive Organization |
License Organization- |
Drug Highest PhasePendingPreclinical |
First Approval Date- |
Regulation- |

| Indication | Highest Phase | Country/Location | Organization | Date |
|---|---|---|---|---|
| Lafora Disease | Preclinical | United States | 05 Nov 2018 |





