Drug Type AAV based gene therapy |
Synonyms- |
Target |
Mechanism SMAD7 modulators(Mothers against decapentaplegic homolog 7 modulators), Gene transference |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Muscular Dystrophy, Duchenne | Preclinical | FR | - |