Drug Type AAV based gene therapy |
Synonyms AAV-based gene therapy (LYSOGENE) |
Target |
Mechanism DGKK stimulants(diacylglycerol kinase kappa stimulants), Gene transference |
Therapeutic Areas |
Active Indication- |
Inactive Indication |
Originator Organization |
Active Organization- |
Inactive Organization |
Drug Highest PhasePendingDiscovery |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Fragile X Syndrome | Discovery | FR | 11 Jun 2021 |