Last update 21 Dec 2024
Ocular Gene Therapies (Ascidian Therapeutics)
Last update 21 Dec 2024
Overview
Basic Info
Drug Type AAV based gene therapy |
Synonyms AAV8_ABCA4 RNA Exon Editor (Ascidian Therapeutics) |
Target |
Mechanism ABCA4 stimulants(ATP binding cassette subfamily A member 4 stimulants) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization  Ascidian Therapeutics, Inc.Startup |
Active Organization Ascidian Therapeutics, Inc.Startup |
Inactive Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
RegulationOrphan Drug (US) |
R&D Status
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| Indication | Highest Phase | Country/Location | Organization | Date |
|---|---|---|---|---|
| Stargardt Disease | Preclinical | US |  Ascidian Therapeutics, Inc.Startup | - |
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Clinical Result
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