Drug Type Small molecule drug |
Synonyms- |
Target |
Action modulators |
Mechanism SMN2 modulators(Survival motor neuron protein modulators) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
License Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
Regulation- |
Molecular FormulaC22H23FN6 |
InChIKeyNVRMRBZITQQJFE-UHFFFAOYSA-N |
CAS Registry3017198-62-5 |
| Indication | Highest Phase | Country/Location | Organization | Date |
|---|---|---|---|---|
| Spinal Muscular Atrophy | Preclinical | United States | 30 Jun 2025 |





