Drug Type AAV based gene therapy |
Synonyms utrophin CRISPR/Cas9-gene therapy (University College London/Genethon) |
Target |
Mechanism UTRN activators(Utrophin activators) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Muscular Dystrophy, Duchenne | Preclinical | FR | - | |
Muscular Dystrophy, Duchenne | Preclinical | GB | - |