Drug Type AAV based gene therapy |
Synonyms AAV9-CAG-coh-SGSH, AAV9-hsulfamidase, NAV rAAv9 sulfamidase gene therapy + [1] |
Target |
Action stimulants |
Mechanism SGSH stimulants(N-sulphoglucosamine sulphohydrolase stimulants) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePhase 2 |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Mucopolysaccharidosis III | Phase 2 | - | - |