Drug Type Small molecule drug |
Synonyms- |
Target |
Action modulators |
Mechanism survival of motor neuron 1, telomeric modulators |
Therapeutic Areas |
Active Indication- |
Inactive Indication |
Originator Organization |
Active Organization- |
Inactive Organization |
License Organization- |
Drug Highest PhasePendingDiscovery |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Spinal Muscular Atrophy | Discovery | United States | 03 Apr 2007 | |
Spinal Muscular Atrophy | Discovery | United States | 03 Apr 2007 |