Drug Type AAV based gene therapy |
Synonyms VGN-R08b, VGNR08 |
Target |
Action stimulants |
Mechanism GBA stimulants(Beta-glucocerebrosidase stimulants), Gene transference(Gene transference) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
License Organization- |
Drug Highest PhaseEarly Phase 1 |
First Approval Date- |
RegulationRare Pediatric Disease (United States) |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Gaucher Disease, Type 2 | Phase 1 | China | 01 Mar 2023 |
Not Applicable | - | dofsfnjnhr(kyydzruudw) = ruzrpquvrj urysuxteoa (ygmoygrjtp ) View more | - | 07 May 2024 |