Drug Type AAV based gene therapy |
Synonyms MyoAAV-DUX4 miRNA |
Target |
Mechanism DUX4 gene modulators(Double homeobox protein 4 gene modulators) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Muscular Dystrophy, Facioscapulohumeral | Preclinical | US | 03 Apr 2024 |