Drug Type AAV based gene therapy |
Synonyms adeno-associated virus vector gene therapy (Genethon) |
Target- |
Action- |
Mechanism Gene transference |
Therapeutic Areas |
Active Indication- |
Inactive Indication |
| Indication | Highest Phase | Country/Location | Organization | Date |
|---|---|---|---|---|
| Mucopolysaccharidosis III | Discovery | France | - |





